Gene therapy breakthrough seen in Leber's congenital amaurosis

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Philadelphia-Much progress has been made in the development of gene therapies for retinal dystrophies during the last decade. Albert Maguire, MD

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Cassandra Gorsuch, PhD, chief scientific officer at Precision
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Linda Marbán, PhD, the CEO of Capricor Therapeutics
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Renier Brentjens, MD, PhD, the chair of the department of medicine and the deputy director at Roswell Park Comprehensive Cancer Center
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