John Ligon, MD, on Establishing a Roadmap for CAR-T Fertility Research
March 14th 2024The assistant professor in the department of pediatrics at the University of Florida College of Medicine discussed the importance of involving all relevant providers and patients in research to ensure the right questions are being asked.
John Ligon, MD, on Fertility Outcomes in Patients Who Have Received CAR-T
March 11th 2024The assistant professor in the department of pediatrics at the University of Florida College of Medicine discussed also discussed the need to set standard guidelines regarding potential fertility issues for CAR-T treatment.
Carrie Miceli, PhD, on the Potential of Needle Biopsy Findings to Improve DMD Gene Therapy
March 9th 2024The professor of microbiology, immunology, and molecular genetics at UCLA discussed how a better understanding of treatment impact on a cellular level could help improve future gene therapy approaches.
Paul Melmeyer, MPP, on Advocacy and Progress in Rare Neuromuscular Diseases From a Policy Standpoint
February 29th 2024In observance of Rare Disease Day 2024, the vice president of public policy and advocacy at the Muscular Dystrophy Association discussed advocacy and policy progress regarding rare neuromuscular diseases.