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Solid Biosciences' CPVT Gene Therapy SGT-501 Cleared for Phase 1b Trial
Solid Biosciences' CPVT Gene Therapy SGT-501 Cleared for Phase 1b Trial

July 10th 2025

SGT-501 is intended to address CPVT by providing a full-length, codon-optimized copy of the cardiac calsequestrin gene to the muscle cells of the heart.

Jeffrey Chamberlain, PhD, Professor, Neurology and Medical Genetics, and Adjunct Professor, Biochemistry, and McCaw Endowed Chair of Muscular Dystrophy at University of Washington
Jeffrey Chamberlain, PhD, on the Import of Early Intervention in DMD

July 10th 2025

Around the Helix: Cell and Gene Therapy Company Updates – July 9, 2025
Around the Helix: Cell and Gene Therapy Company Updates – July 9, 2025

July 9th 2025

Derek Jackson, BS, MA, the vice president of cell & gene therapy product development at Pacira, and Kilian Guse, PhD, the vice president of genetic medicine platforms at Pacira
Derek Jackson, BS, MA, and Kilian Guse, PhD, on High-Capacity Adenovirus Vectors for Gene Therapy

July 9th 2025

Jeffrey Chamberlain, PhD, Professor, Neurology and Medical Genetics, and Adjunct Professor, Biochemistry, and McCaw Endowed Chair of Muscular Dystrophy at University of Washington
The Role of Gene Therapy for Patients with Duchenne Muscular Dystrophy

July 9th 2025

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Derek Jackson, BS, MA, the vice president of cell & gene therapy product development at Pacira, and Kilian Guse, PhD, the vice president of genetic medicine platforms at Pacira
Derek Jackson, BS, MA, and Kilian Guse, PhD, on High-Capacity Adenovirus Vectors for Gene Therapy

July 9th 2025

Derek Jackson, BS, MA, the vice president of cell & gene therapy product development at Pacira
Derek Jackson, BS, MA, on Evaluating Gene Therapy PCRX-201 for Osteoarthritis of the Knee

July 8th 2025

Survival Outcomes Found to Be Comparable for Axi-Cel, Liso-Cel, and Tisa-Cel in Real-World DLBCL Data
Survival Outcomes Found to Be Comparable for Axi-Cel, Liso-Cel, and Tisa-Cel in Real-World DLBCL Data

June 29th 2025

Peter Cook, PhD, a senior research scientist at Seattle Children’s Research Institute
Exploring DARIC CAR T Cells for Autoimmune Indications

June 23rd 2025

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