Lysosomal Disorders

Fabry Disease Gene Therapy Clinical Trial Moves Onto Dosing Second Cohort

The FDA recently cleared Freeline Therapeutics to begin treating patients in the United States.

Treating Autoimmune Diseases With Smarter Cell Therapies

Karen Walker, chief technology officer, Kyverna Therapeutics, discussed the company’s CAR T-cell and regulatory T-cell technologies.

Around the Helix: Cell and Gene Therapy Company Updates – October 5, 2022

Catch up on the latest news, breakthroughs, and announcements from biotechnology companies making advancements in cell and gene therapies.