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Neurology

Around the Helix: Cell and Gene Therapy Company Updates – October 5, 2022

Catch up on the latest news, breakthroughs, and announcements from biotechnology companies making advancements in cell and gene therapies.

Gene Therapy Trial Makes Headway in Canavan Disease

Data from the first 3 of the 8 patients dosed indicates that the patients improved on the GMFM and the MSEL.

Solid Bio Adds Friedreich Ataxia to Pipeline With Aavanti Acquisition

Solid has also pivoted from developing SGT-001 to SGT-003 for treating Duchene muscular dystrophy.