
Serious adverse events of reduced visual acuity and eye inflammation were observed in 2 clinical trials.

Serious adverse events of reduced visual acuity and eye inflammation were observed in 2 clinical trials.

The low-dose cohort of RP-A501 conferred cardiac LAMP2B transgene expression.

A new study presented at ASGCT found that patients with indications of hemostatic efficacy experienced few adverse effects with gene therapy treatment BAY 2599023.