Two Gene Therapies Fix Fault in Sickle Cell Disease and ß-thalassemia
Two gene therapy techniques in separate, concurrently published trials demonstrate clinical success in mitigating monogenic hemoglobinopathies.
Multiple Sclerosis Stem Cell Transplant Compared to Disease-Modifying Therapy
In a rare clinical trial, stem cell transplantation appeared to provide greater protection against MS progression than DMT.