Paul Wuh-Liang Hwu, MD, PhD

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The professor from National Taiwan University Hospital discussed his work in improving diagnoses in Pompe disease and AADC deficiency.

The professor from National Taiwan University Hospital discussed the importance of Rare Disease Day for raising awareness.

The professor from National Taiwan University Hospital discussed gene therapy studies in AADC deficiency, Parkinson disease, SMA, and Pompe disease.

The professor from National Taiwan University Hospital discussed the benefits of delivering gene therapy directly to the putamen in AADC deficiency.

The professor from National Taiwan University Hospital discussed the challenges of working with a rare disease.

The professor from National Taiwan University Hospital discussed further research he would like to do with the gene therapy PTC-AADC.

The professor from National Taiwan University Hospital discussed the mechanism of gene therapy in AADC deficiency.

The professor from National Taiwan University Hospital discussed 3 studies of PTC-AADC for AADC deficiency.