News|Articles|August 3, 2025

Spinal Muscular Atrophy Month 2025: Looking Back at News and Expert Insights

In observance of Spinal Muscular Atrophy Awareness Month, held annually in August, we took a look back at the past year's news in gene and cell therapy for SMA.

According to Cure SMA, spinal muscular atrophy (SMA), which is caused by mutations in the survival motor neuron gene 1 (SMN1), occurs in approximately 1 in 15,000 births in the United States.¹ The condition leads to muscle weakness that can range from debilitating to fatal. It can affect patients of any race or gender.