Associate chair, pediatrics and director, Powell Gene Therapy Center, University of Florida
Barry J Byrne, MD, PhD, on the Potential of Directed Evolution to Improve AAV Gene Therapy
The chief medical advisor of the Muscular Dystrophy Association discussed how directed evolution may help develop AAV capsids better suited for treating neuromuscular diseases.
Barry J Byrne, MD, PhD, on Overcoming the Hurdles Presented by Immunity to AAV Vectors
The chief medical advisor of the Muscular Dystrophy Association discussed research he is working on with the goal of increasing eligibility for gene therapies and opening the door to redosing.
Barry J Byrne, MD, PhD, on MDA Care Centers and the Upcoming Clinical & Scientific Conference
The chief medical advisor of the Muscular Dystrophy Association discussed what seasoned clinicians and newcomers to the field alike can look forward to at the 2024 MDA Meeting.
Research Needs in Pompe Disease: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed unmet needs that remain in Pompe disease.
Improving Rare Disease Awareness: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed the importance of Rare Disease Day.
Access to Gene Therapies for Rare Diseases: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed improving access to gene therapies for patients with rare diseases worldwide.
Safety Concerns With Gene Therapies: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed adverse events in gene therapies.
Cellular, Tissue, and Gene Therapies AdComm Meeting Takeaways: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed the recent meeting of the FDA Cellular, Tissue, and Gene Therapies Advisory Committee.
Gene Therapy for Pompe Disease: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed gene therapy programs being conducted for Pompe disease.
