Associate chair, pediatrics and director, Powell Gene Therapy Center, University of Florida
Research Needs in Pompe Disease: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed unmet needs that remain in Pompe disease.
Improving Rare Disease Awareness: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed the importance of Rare Disease Day.
Access to Gene Therapies for Rare Diseases: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed improving access to gene therapies for patients with rare diseases worldwide.
Safety Concerns With Gene Therapies: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed adverse events in gene therapies.
Cellular, Tissue, and Gene Therapies AdComm Meeting Takeaways: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed the recent meeting of the FDA Cellular, Tissue, and Gene Therapies Advisory Committee.
Gene Therapy for Pompe Disease: Barry Byrne, MD, PhD
The director of the Powell Gene Therapy Center at the University of Florida discussed gene therapy programs being conducted for Pompe disease.
