Researchers Highlight Potential of Gene Editing in Inherited Retinal Diseases
Studies have demonstrated positive data that suggest in vivo gene editing will be the future treatment paradigm for retinal diseases.
New Genetic Target May Hold Promise in Treating Blindness
The SARM1 gene is a key driver in the damage that ultimately leads to impaired vision.
Cell Therapy a Promising Option in Corneal Endothelial Disease
The cell therapy yielded improvements in visual acuity and central corneal thickness.
Collaboration boosts AAV vectors for gene therapy
Avalanche Biotechnologies Inc. and Lonza have announced a manufacturing collaboration focused on process development and scale-up efforts for the manufacturing of adeno-associated viral (AAV) vectors for gene therapy.