CGTLive’s Weekly Rewind – June 23, 2023
Review top news and interview highlights from the week ending June 23, 2023.
Welcome to CGTLive™’s Weekly Rewind! We’ve compiled 5 highlights from this week’s coverage of advances in gene and cell therapies, including FDA actions, notable research, and interviews with experts across the field.
1. FDA Approves Sarepta's Landmark DMD Gene Therapy Elevidys
Delandistrogene moxaparvovec treatment will reportedly cost $3.2 million.
2. Nikhil Munshi, MD, on Final Data on Cilta-Cel in Multiple Myeloma From CARTITUDE-1
The associate professor from Dana Farber Cancer Center and Harvard Medical School discussed continued efficacy and safety data presented at the 2023 EHA Meeting.
3. 2023 World Sickle Cell Day: The Home Stretch for Gene Therapy in SCD?
More work remains to be done to improve accessibility to populations and countries that have the highest unmet need with SCD treatment.
4. Maria Pia Morelli, MD, PhD, on Promising Efficacy of Sleeping Beauty TCR-T Therapy in Solid Tumors
The assistant professor at MD Anderson Cancer Center discussed new data she presented at the 2023 ASCO Meeting.
5. Patient Death Prompts Hold on Arcellx’s CART-ddBCMA for R/R Multiple Myeloma
The company believes that limitations on bridging therapies were a contributing factor to the death.
News and Expert Insights in Hemophilia Gene Therapy for Bleeding Disorders Awareness Month 2025
March 9th 2025In observance of Bleeding Disorders Awareness Month, held annually in March, catch up on some of the latest news and expert insights in gene therapy for hemophilia, which is among the most common of these disorders.
