CGTLive’s Weekly Rewind – June 23, 2023


Review top news and interview highlights from the week ending June 23, 2023.

Welcome to CGTLive™’s Weekly Rewind! We’ve compiled 5 highlights from this week’s coverage of advances in gene and cell therapies, including FDA actions, notable research, and interviews with experts across the field.

1. FDA Approves Sarepta's Landmark DMD Gene Therapy Elevidys

Delandistrogene moxaparvovec treatment will reportedly cost $3.2 million.

2. Nikhil Munshi, MD, on Final Data on Cilta-Cel in Multiple Myeloma From CARTITUDE-1

The associate professor from Dana Farber Cancer Center and Harvard Medical School discussed continued efficacy and safety data presented at the 2023 EHA Meeting.

3. 2023 World Sickle Cell Day: The Home Stretch for Gene Therapy in SCD?

More work remains to be done to improve accessibility to populations and countries that have the highest unmet need with SCD treatment.

4. Maria Pia Morelli, MD, PhD, on Promising Efficacy of Sleeping Beauty TCR-T Therapy in Solid Tumors

The assistant professor at MD Anderson Cancer Center discussed new data she presented at the 2023 ASCO Meeting.

5. Patient Death Prompts Hold on Arcellx’s CART-ddBCMA for R/R Multiple Myeloma

The company believes that limitations on bridging therapies were a contributing factor to the death.

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Zheng-Yi Chen, DPhil, on International Collaboration on Clinical Trials
Maria Escolar, MD, the chief medical officer of Forge Biologics
Leigh Ramos-Platt, MD, on Allowing Access and Ensuring Preparation for Gene Therapies
Erika Fullwood Augustine, MD, MS, the associate chief science officer of the Kennedy Krieger Institute
Maria Escolar, MD, the chief medical officer of Forge Biologics
Casey Maguire, PhD, associate professor of neurology and associate investigator of neurology, Harvard Medical School
Evan Weber, PhD, an assistant professor of pediatrics at Children's Hospital of Philadelphia
Shankar Ramaswamy, MD, the cofounder, chairman, and CEO of Kriya Therapeutics
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