Zolgensma Gene Therapy Data Manipulation, GRF6019 Phase 2 Results in Mild to Moderate Alzheimer, Mind Moments Podcast
Neurology News Network for the week ending August 10, 2019.
This week, Neurology News Network covered the statement that the FDA released announcing that early testing of Zolgensma was manipulated, positive top-line data from a phase 2 studying GRF6019 for mild-to-moderate Alzheimer disease, and the first episodie of NeurologyLive's Mind Moments podcast (transcript below).
Jenna:
Welcome to Neurology News Network. I’m Jenna Payesko. Let’s get into the news from this week.
The
AveXis Inc., a subsidiary of Novartis, informed the agency of the data manipulation on June 28, just over a month following the therapy's momentous approval. Of the entirety of the data submitted and reviewed by the agency, at this time, the manipulation concerns are confined to only a small portion which was performed in animals and submitted in the BLA. Thus far, the manipulated information does not change the FDA’s positive assessment of data from the human clinical trials.
NeurologyLive is proud to introduce the first episode of the Mind Moments podcast, your resource for expert insights on the diagnosis, treatment, and management of neurologic disorders. It will feature exclusive interviews with leaders in the field discussing the latest research and disease management strategies across the breadth of neurology, including epilepsy, multiple sclerosis, Parkinson disease, dementia, sleep disorders, and more.
For more direct access to expert insight, head to neurologylive.com. This has been Neurology News Network. Thanks for watching.
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