HCP Live
Contagion LiveCGT LiveNeurology LiveHCP LiveOncology LiveContemporary PediatricsContemporary OBGYNEndocrinology NetworkPractical CardiologyRheumatology Netowrk
Hemgenix First Gene Therapy Approved for Hemophilia B

A marketing authorization application for etranacogene dezaparvovec is currently under review by the EMA.

Legend Biotech Brings SCLC CAR T to Trials

The IND clearance comes after Legend terminated another clinical trial in T-cell lymphoma in July 2022.

Omidubicel PDUFA Date Extended to May 2023

Omidubicel’s BLA was originally accepted for priority review in August of this year.

Targeting Hematological Malignancies With Autologous and Allogeneic Cell Therapies

Thomas Willemsen, president and chief executive officer, Tessa Therapeutics, discussed the company’s technologies and 2023 milestones.

MPS Type IIIA Gene Therapy Trial Fails Primary Endpoint

Statistically significant improvements in cognitive development were only seen in the cohort of patients younger than 30 months.

Upstaza Approved for AADC Deficiency in UK

The gene therapy was approved in the European Union earlier this year.