
The professor of genetics at Federal University of Rio Grande do Sul discussed updated data from the CAMPSIITE trial.
The professor of genetics at Federal University of Rio Grande do Sul discussed updated data from the CAMPSIITE trial.
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Preliminary data from an ongoing clinical trial suggest that AVR-RD-04 has been well-tolerated.
In a mouse model of MPS II, IDS.ApoEII effected completely normalized brain pathology and behavior.
Review top news and interview highlights from the week ending September 16, 2022.
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iECURE is planning to submit an IND for GTP-506 in mid-2023.
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Immusoft plans to begin the phase 1 clinical trial of ISP-001 before the end of 2022.
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The in vivo genome-editing therapy is the first gene therapy to be evaluated in a clinical trial for preventing HAE attacks.
RGX-121 was well-tolerated across all 3 of the dose cohorts with no treatment-related serious adverse events reported.
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Updated data from the STAAR clinical trial were presented at the SSIEM Annual Meeting.
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iECURE and the University of Pennsylvania Gene Therapy Program have collaborated to develop the GTP-506 program.
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Review top news and interview highlights from the week ending August 19, 2022.
The pheEDIT clinical trial initiated in June 2022.
Catch up on the latest news, breakthroughs, and announcements from biotechnology companies making advancements in cell and gene therapies.
Preclinical data showed a reduction of Gys1 mRNA and protein of more than 80% in multiple skeletal tissues.
Preclinical data showed hARSA activity levels in the brain that are predictive of functional improvements.
Review top news and interview highlights from the week ending August 12, 2022.
Catch up on the latest news, breakthroughs, and announcements from biotechnology companies making advancements in cell and gene therapies.