Keith Fargo, PhD, on Potential Treatment Avenues for Charcot-Marie-Tooth

The chief scientific officer of the CMT Research Foundation discussed investigative cell and gene therapy approaches for treating CMT.

CGTLive’s Weekly Rewind – June 17, 2022

Review top news and interview highlights from the week ending June 17, 2022.

Vutrisiran Approved for hATTR Amyloidosis

The approval came earlier than the recently extended PDUFA date of July 24, 2022.