Karmen Trzupek discusses the complex interpretation of genetic test results
In his gene therapy break with the experts , Mark Pennesi compared genetic testing for IRDs to fishing
Dominik Fischer presents gene therapy proof-of-concept results in choroideremia
Vinit Mahajan explains that RPE65 mutation subtype was unrelated to outcomes in the Luxturna gene therapy trial
Christine Kay summarizes her jam packed session on gene therapy
Birgit Lorenz looks ahead to ISGEDR 2019 where gene therapy will be a major topic
Exploring New Pathways in Muscular Dystrophy Research: From Fibrosis to Function
April 30th 2025Matthew Alexander, PhD, a neuromuscular expert, discussed the evolving landscape of targeted therapies in muscular dystrophies, from fibrosis and glycosylation to combination strategies with gene therapy.