Karmen Trzupek discusses the complex interpretation of genetic test results
In his gene therapy break with the experts , Mark Pennesi compared genetic testing for IRDs to fishing
Dominik Fischer presents gene therapy proof-of-concept results in choroideremia
Vinit Mahajan explains that RPE65 mutation subtype was unrelated to outcomes in the Luxturna gene therapy trial
Christine Kay summarizes her jam packed session on gene therapy
Birgit Lorenz looks ahead to ISGEDR 2019 where gene therapy will be a major topic
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Jeffrey Chamberlain, PhD, on the Import of Early Intervention in DMD
July 10th 2025The McCaw Endowed Chair of Muscular Dystrophy at University of Washington, discussed how comprehensive care for DMD patients involves early diagnosis, steroid treatment, consideration of mutation-specific therapies, and more.