One-year KYSA-8 and KYSA-6 data showed durable miv-cel benefit in SPS and gMG, supporting Kyverna's rolling BLA submission targeted for Q4 2026.
|Articles|November 13, 2018
AAO Gene Therapy Street Team
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Karmen Trzupek discusses the complex interpretation of genetic test results
In his gene therapy break with the experts , Mark Pennesi compared genetic testing for IRDs to fishing
Dominik Fischer presents gene therapy proof-of-concept results in choroideremia
Vinit Mahajan explains that RPE65 mutation subtype was unrelated to outcomes in the Luxturna gene therapy trial
Christine Kay summarizes her jam packed session on gene therapy
Birgit Lorenz looks ahead to ISGEDR 2019 where gene therapy will be a major topic
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