CGTLive®’s Weekly Rewind – April 12, 2024

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Review top news and interview highlights from the week ending April 12, 2024.

CGTLive®’s Weekly Rewind - April 12, 2024.

CGTLive®’s Weekly Rewind

Welcome to CGTLive®’s Weekly Rewind! We’ve compiled 5 highlights from this week’s coverage of advances in gene and cell therapies, including FDA actions, notable research, and interviews with experts across the field.

1. BrainStorm Reaches Accord With FDA on New Phase 3b Trial Design for ALS Cell Therapy NurOwn

The 2-part, multicenter BCT-006-US trial will seek to enroll patients who are in the earlier stages of ALS.

2. Frederick “Eric” Arnold, PhD, on Investigating MARK3 Polyadenylation and Microtubule Dynamics in ALS Models

The postdoctoral scholar at University of California – Irvine discussed further questions he is continuing to investigate.

3. CAR TEAM Cells Show Promise in Multiple Preclinical Models of Pancreatic Cancer

The cells showed activity toward PDAC cells as well as cancer-associated fibroblasts, which may address challenges with the tumor microenvironment.

4. Amar Kelkar, MD, on Assessing Price and Value for Cell and Gene Therapies

The stem cell transplantation physician at the Dana-Farber Cancer Institute discussed how to look at the value therapies provide and how to improve the cost-effectiveness of their use.

5. Aurion Biotech’s ABA-1 Clinical Trial for Corneal Edema Cell Therapy AURN001 Doses First Canadian Patient

AURN001 consists of allogeneic human corneal endothelial cells referred to as “neltependocel” and Y-27632, a small molecule drug.

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Mark Hamilton, MD, PhD, a hematology-oncology and bone marrow transplant (BMT) cell therapy fellow at Stanford University
Barry J Byrne, MD, PhD, the chief medical advisor of MDA and a physician-scientist at the University of Florida
Barry J Byrne, MD, PhD, the chief medical advisor of MDA and a physician-scientist at the University of Florida
Sarah Larson, MD, the medical director of the Immune Effector Cell Therapy Program in the Division of Hematology/Oncology at David Geffen School of Medicine at University of California, Los Angeles (UCLA)
Manali Kamdar, MD, the associate professor of medicine–hematology and clinical director of lymphoma services at the University of Colorado
Manali Kamdar, MD, the associate professor of medicine–hematology and clinical director of lymphoma services at the University of Colorado
Ben Samelson-Jones, MD, PhD, assistant professor pediatric hematology, Perelman School of Medicine, University of Pennsylvania and Associate Director, Clinical In Vivo Gene Therapy, Children’s Hospital of Philadelphia
Manali Kamdar, MD, the associate professor of medicine–hematology and clinical director of lymphoma services at the University of Colorado
Steven W. Pipe, MD, a professor of pediatric hematology/oncology at CS Mott Children’s Hospital
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