CGTLive®’s Weekly Rewind – April 12, 2024

News
Article

Review top news and interview highlights from the week ending April 12, 2024.

CGTLive®’s Weekly Rewind - April 12, 2024.

CGTLive®’s Weekly Rewind

Welcome to CGTLive®’s Weekly Rewind! We’ve compiled 5 highlights from this week’s coverage of advances in gene and cell therapies, including FDA actions, notable research, and interviews with experts across the field.

1. BrainStorm Reaches Accord With FDA on New Phase 3b Trial Design for ALS Cell Therapy NurOwn

The 2-part, multicenter BCT-006-US trial will seek to enroll patients who are in the earlier stages of ALS.

2. Frederick “Eric” Arnold, PhD, on Investigating MARK3 Polyadenylation and Microtubule Dynamics in ALS Models

The postdoctoral scholar at University of California – Irvine discussed further questions he is continuing to investigate.

3. CAR TEAM Cells Show Promise in Multiple Preclinical Models of Pancreatic Cancer

The cells showed activity toward PDAC cells as well as cancer-associated fibroblasts, which may address challenges with the tumor microenvironment.

4. Amar Kelkar, MD, on Assessing Price and Value for Cell and Gene Therapies

The stem cell transplantation physician at the Dana-Farber Cancer Institute discussed how to look at the value therapies provide and how to improve the cost-effectiveness of their use.

5. Aurion Biotech’s ABA-1 Clinical Trial for Corneal Edema Cell Therapy AURN001 Doses First Canadian Patient

AURN001 consists of allogeneic human corneal endothelial cells referred to as “neltependocel” and Y-27632, a small molecule drug.

Newsletter

Stay at the forefront of cutting-edge science with CGT—your direct line to expert insights, breakthrough data, and real-time coverage of the latest advancements in cell and gene therapy.

Recent Videos
Prerna Mewawalla, MD, medical director of Apheresis and a hematologist-oncologist in the Division of Hematology and Cellular Therapy at Allegheny Health Network, as well as an associate professor at the Drexel University College of Medicine
Surbhi Sidana, MD, an assistant professor of medicine, bone marrow transplantation, and cellular therapy at Stanford
Damien Maura, PhD, a senior scientist at Voyager Therapeutics
© 2025 MJH Life Sciences

All rights reserved.