Review top news and interview highlights from the week ending May 24, 2024.
CGTLive®’s Weekly Rewind
Welcome to CGTLive®’s Weekly Rewind! We’ve compiled 5 highlights from this week’s coverage of advances in gene and cell therapies, including FDA actions, notable research, and interviews with experts across the field.
Tab-Cel is approved under the name Ebvallo in Europe, Switzerland, and United Kingdom.
The Associate Professor of Neurology at Keck School of Medicine of USC discussed her talk on preparing for gene therapy administration.
Excision is evaluating a higher dose in a second cohort as well as exploring alternative, potentially redosable, delivery methods.
The associate chief science officer of the Kennedy Krieger Institute discussed an aspect of clinical trial design highly relevant to gene therapy development for rare diseases.
Most participants had improved or stable cognitive function in a proof-of-concept study.
Will the CMS CGT Model Support Patient Access to Sickle Cell Disease CGTs?
July 25th 2024Cell and gene therapies can transform the paradigm of care for patients with chronic, complex conditions, but these therapies come at an up-front cost of several million dollars per treatment, complicating the pipeline of access to them.