Lysosomal Disorders

The CGTLive Lysosomal Disorders specialty topic page contains video interviews with key opinion leaders discussing the most relevant FDA actions, clinical guideline updates, and clinical trial findings related to cell therapies, gene therapies, and engineered and regenerative medicines developed for Lysosomal storage diseases. It also houses the most up-to-date clinical news coverage in the field of gene and cell therapy for diseases related to lysosomal storage and dysfunction.

Latest News

CGTLive®’s Weekly Rewind
CGTLive®’s Weekly Rewind – July 18, 2025

July 18th 2025

Review top news and interview highlights from the week ending July 18, 2025.

Five Advanced Therapeutics to Watch in 2H 2025
Five Advanced Therapeutics to Watch in 2H 2025

July 17th 2025

Around the Helix: Cell and Gene Therapy Company Updates – July 16, 2025
Around the Helix: Cell and Gene Therapy Company Updates – July 16, 2025

July 16th 2025

Heather Lau, MD, MS
Ultragenyx’s MPS IIIA Gene Therapy UX111 Met With CRL

July 14th 2025

CGTLive®’s Weekly Rewind
CGTLive®’s Weekly Rewind – July 11, 2025

July 11th 2025

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