Lysosomal Disorders

The CGTLive Lysosomal Disorders specialty topic page contains video interviews with key opinion leaders discussing the most relevant FDA actions, clinical guideline updates, and clinical trial findings related to cell therapies, gene therapies, and engineered and regenerative medicines developed for Lysosomal storage diseases. It also houses the most up-to-date clinical news coverage in the field of gene and cell therapy for diseases related to lysosomal storage and dysfunction.

Latest News

Long-Term Case Series Supports CAR-T Therapy in Autoimmune Disease
Long-Term Case Series Supports CAR-T Therapy in Autoimmune Disease

March 28th 2024

A 2-year evaluation of a small cohort of patients with systemic lupus erythematosus, idiopathic inflammatory myositis, and systemic sclerosis showed safety and efficacy which were supportive of additional clinical trials.

Around the Helix: Cell and Gene Therapy Company Updates – March 27, 2024
Around the Helix: Cell and Gene Therapy Company Updates – March 27, 2024

March 27th 2024

CGTLive®’s Weekly Rewind – March 22, 2024
CGTLive®’s Weekly Rewind – March 22, 2024

March 22nd 2024

Around the Helix: Cell and Gene Therapy Company Updates – March 20, 2024
Around the Helix: Cell and Gene Therapy Company Updates – March 20, 2024

March 20th 2024

Phase 3 Trial Seeks to Continue Supporting Arsa-Cel Gene Therapy for MLD
Phase 3 Trial Seeks to Continue Supporting Arsa-Cel Gene Therapy for MLD

March 18th 2024

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