Carol Miao, PhD, on Delivering Gene Editing Tools With Nonviral Methods in Hemophilia A ModelsMay 28th 2023
The principal investigator at Seattle Children’s Research Institute discussed her lab’s preclinical research on nonviral delivery methods for gene editing tools in the context of treating hemophilia A.
Carol Miao, PhD, on Exploring New Delivery Methods for Gene Replacement Therapy and Gene EditingMay 26th 2023
The principal investigator at Seattle Children’s Research Institute discussed the preclinical research on delivery methods for genomic medicines that her lab presented at ASGCT’s 2023 meeting.
Jennifer Gori, PhD, on the Potential of a Prime Editing Approach in Treating Chronic Granulomatous DiseaseMay 18th 2023
The vice president of research at Prime Medicine discussed a preclinical study on a novel autologous HSCT treatment that was presented at ASGCT’s 2023 annual meeting.
Krystof Bankiewicz, MD, PhD, on Dialing Back Progression of Parkinson Disease With GDNF Gene TherapyMay 17th 2023
The professor at Ohio State University and University of California – San Francisco discussed updated data from a phase 1 study of GDNF gene therapy in patients with PD.